Cure SMA - Connecticut Chapter

More treatment progress!

Scholar Rock has resubmitted its Biologics License Application (BLA) to the U.S. Food and Drug Administration for apitegromab, an investigational therapy for spinal muscular atrophy.

Scholar Rock anticipates FDA acceptance of the BLA within 30 days of resubmission and a review period of up to six months from the date of resubmission.

Cure SMA will continue to monitor progress and share updates with the community.

Click the link to read the full update: https://www.curesma.org/scholar-rock-resubmits-biologics-license-application-bla-for-apitegromab-to-the-fda/

Incredible news for the SMA Community!

Biogen today announced that it has received approval from the U.S. Food and Drug Administration (FDA) for the High Dose regimen of SPINRAZA to treat people living with SMA. With broad label approval for all those living with SMA, this is an excellent result for the SMA community.

This FDA approval marks another important step forward in the ongoing effort to treat and manage SMA. The High Dose regimen of SPINRAZA has the potential to provide additional benefit for those currently receiving treatment, offering new possibilities for improved outcomes and quality of life. Cure SMA is committed to working closely with Biogen, healthcare providers, and the SMA community to support timely education and access to this new dosing option, in alignment with its approved use.

To learn more, please visit: https://www.curesma.org/biogen-receives-fda-approval-of-high-dose-spinraza-for-the-treatment-of-sma/

The picnic is just a few days away and we're getting really excited to see everyone!
Here's a suggested packing list (obviously you don't need to bring EVERYTHING. These are just some ideas):
Hydration (for yourself)
Sustenance (to share)
Beach towels
Bathing suits
Swim gear
Sand toys
Sunscreen
Beach umbrella
Kite, bubbles, other fun stuff
A change of clothes

SAVE THE DATE: CT Cure SMA picnic is 8/24 at Camp Harkness in Pavilion 1! More information to come!

Stock up on your favorite Cure SMA Swag in time for the holidays with this Cyber Monday deal!

This Cyber Monday, you can get great deals on all Cure SMA swag!

Orders over $50 will automatically receive a FREE Cure SMA custom die cut birch ornament, a Square Sticker Pack, AND a Cure SMA Cookie Cutter ($33 value) while supplies last! 💜🧡

Receive 25% off your entire order with discount code "CYBERMONDAY" at checkout.

https://curesmaorg.myshopify.com