ASA - Angelman Syndrome Alliance

Today, representatives from 11 international Angelman syndrome organisations met to discuss future priorities for - Angelman syndrome alliance. Thank you Conny & e.V for hosting the meeting in Hamburg.

Together we are stronger.

ASA - Angelman Syndrome Alliance Angel - Associação Síndrome de Angelman Portugal Association Française du Syndrome d'Angelman Angelman Syndrome Ireland ORSA Organizzazione Sindrome di Angelman Asociace genové terapie, z.s. A.S.A. ASOCIACION SINDROME DE ANGELMAN - ESPAÑA Angelman e.V. Angelman Syndroom NL Angelman UK Mizukawa Masako Angelman Verein Österreich

www.angelmanalliance.org

💙 Angelman Syndrome Phase 3 Trials – Community Update 💙

Earlier this month, Foundation for Angelman Syndrome Therapeutics and ASA - Angelman Syndrome Alliance co-hosted a community webinar to share updates on the ongoing Phase 3 trials for Ultragenyx (GTX-102) and Ionis (ION-582).

Families will find practical information on study designs, age groups, timelines, and what participation in a trial may involve.

❗️Every child and family is unique. Clinical trials are still evaluating investigational medicines, and participation is a deeply personal decision. Please discuss any questions with your doctor or medical team before considering enrollment.

You can read more about it ⬇️.
https://angelmanalliance.org/community-update-phase-3-trials-ultragenyx-ionis/

📺 You can watch the full webinar here: https://youtu.be/TenTbLp9pIk

Angelman Syndrome Phase 3 Clinical Trial Update - hosted by FAST & ASA ANGELMAN SYNDROME PHASE 3 TRIALS — COMMUNITY UPDATE (Webinar recorded: 4 Sep 2025)WHO HOSTED• FAST (Foundation for Angelman Syndrome Therapeutics): \$60M+ in...